Stem cell / gene therapy success in vitro

Researchers at the Salk Intitute for Biological Studies have demonstrated that a technology to correct the genetic defect in human disease and induce cell differentiation at the site of the manifested disease is feasible, an achievement demonstrated previously only in mice.
 
In the May 31, 2009, edition of Nature, Salk reseachers published their findings for the research, which applied the method to a blood-related disorder called Fanconi’s anemia. (See "Combined stem cell-gene therapy approach cures human genetic disease in vitro" at link.
 
This development, although still only at the in vitro stage, is a remarkable one, since it demonstrates a synthesis of understanding between genetics and cell biology that is a harbinger of tremendous future clinical successes. But, lest the jaded investor or other biotech follower (who has countless times heard in vain of similar portentous milestones) fear that this, too, is a development that is of only passing significance, it should be noted that this development bears greater impact due to the level of science demonstrated and that it has been made by Salk Institute and published in Nature, neither of which should be underestimated.
 
Personally, whenever I note a development that has both "gene therapy" and "cell therapy" in the title, my senses are alerted to the great prospect (not guarantee) of what will follow.
 

Posted via email from medmarket’s posterous

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